Unanswered Questions Remain in Gene Therapy
Industry News & Research
A recent commentary published in the journal Haemophilia, posits that while clinical trials for hemophilia gene therapy approach conclusion, there remain significant unanswered…
Sanofi Publishes Updates to BIVV001 Trial
Industry News & Research
Sanofi recently announced results from their phase 1/2a EXTEN-A trial for their investigational therapy BIVV001, which were published in the New England Journal…
Hemophilia B Therapy to be Discontinued
Industry News & Research
CSL Behring recently announced that they are discontinuing Mononine®, the company’s human plasma-derived factor therapy indicated for the prevention and control of…
NHF’s Board of Directors Meeting
Industry News & Research
The National Hemophilia Foundation will be holding our quarterly Board of Directors meeting on Saturday, October 10th at 9:00 AM EDT. The Board…
Genentech Provides Updates on Hemlibra Product Particles
Industry News & Research
In the fall of last year Genentech reported that during a routine examination of batches of Hemlibra®, they found translucent particles composed…
NHF, HFA and Hemophilia Alliance Continue Push for Information on Stimate Recall
Industry News & Research
The National Hemophilia Foundation (NHF) and Hemophilia Federation of America (HFA) continue to follow up on issues arising from the recent recall of Stimate (desmopressin)…
New MASAC Recommendations Focus on Offsite Hemostasis Screening and Treatment
Industry News & Research
The National Hemophilia Foundation’s (NHF) Medical and Scientific Advisory Council (MASAC) issued two new documents, which were adopted by NHF’s Board of…
Mental Health During Coronavirus
Industry News & Research, COVID-19 / Coronavirus, Uncategorized
by: Debbie de la Riva The collective pursuit to control the spread of coronavirus has resulted in an enormous challenge for the…
What to Do if You Miss Your Child’s Annual Exam
Living with a Bleeding Disorder
Routine healthcare visits are being held up because of the pandemic, so many parents are missing their children’s annual hemophilia treatment center…
NHF’s 2020 Bleeding Disorders Conference Available On Demand Through September 30!
Industry News & Research
NHF’s Bleeding Disorders Conference was fully virtual this year and included more than 50 sessions. Those sessions are all available on-demand until…
BioMarin’s New Clinical Study to Focus on Antibody Development to AAVs
Industry News & Research
Last month, BioMarin learned that approval for their investigational hemophilia A gene therapy was not forthcoming but would in fact be delayed…
Mylan Initiates Voluntary Nationwide Recall of Four Lots of Tranexamic Acid Injection, USP Due to Carton Label Mix-Up
Industry News & Research
On September 1, 2020, NHF and HFA learned that Mylan N.V. is conducting a voluntary nationwide recall of four lots of Tranexamic Acid Injection,…