News

The Low Cost of Being Female with a Bleeding Disorder?

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

Female hemophilia A patients and carriers have more frequent bleeds than males, yet a smaller proportion receive factor to prevent or stop them, a U.S….

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Now Enrolling: Own Your Path

Industry News & Research

Are you a male, 18-29 years old, and on a prophy regimen for hemophilia treatment? You may qualify for a new program!…

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Four New Documents from MASAC

Industry News & Research

The new guidelines cover recommendations for physical therapy, gene therapy readiness, vaccine guidance, and treatment. Download here. Source: National Hemophilia Foundation

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New in Research: Updates on the “My Life Our Future” Project

Industry News & Research

Learn how this project from NHF, the American Thrombosis and Hemostasis Network, Bloodworks Northwest, and Bioverativ/Sanofi helped inform people with hemophilia on…

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Inhibitor Risk Paper Informed by Genotyping Project

Industry News & Research

Between 2013-2017, the “My Life Our Future” (MLOF) project offered eligible individuals with hemophilia free genotyping, which is historically hard to access,…

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Important: Action Needed Regarding Medicaid and Badgercare Eligibility

Advocacy & Legislation, Industry News & Research

As you may have heard, the Medicaid and CHIP (called Badgercare in Wisconsin) programs are re-starting eligibility reviews. Community members may receive…

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FDA Requests Additional Information on Concizumab from Novo Nordisk

Industry News & Research

The company received a Complete Response Letter from the FDA seeking more information relevant to their BLA for concizumab. Novo Nordisk has…

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Updates on Generic Desmopressin Product

Industry News & Research, Uncategorized

Desmopressin has the capacity to boost both factor VIII and von Willebrand factor levels. In July 2020 Ferring Pharmaceuticals suspended manufacturing of…

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New Survey Spotlights Ongoing Concerns for People Living with Hemophilia B

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

Carefully controlled schedules. Undercurrents of uncertainty. Persistent pain. People who are living with hemophilia B, and those who love them, face a…

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HTCs Participate in New CDC Community Counts Data Collection for COVID-19

COVID-19 / Coronavirus, Industry News & Research

Patients with bleeding orders may be asked some new questions during their next comprehensive clinic visit. COVID-19 information will now be collected…

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Sanofi Announces Publication of Two Phase 3 Fitusiran Trials

Industry News & Research, Uncategorized

Fitusiran is being investigated for the prophylactic treatment of adults and adolescents with hemophilia A or B. Sanofi recently announced that results…

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Hemochromatosis Classification: Update and Recommendations by the BIOIRON Society

Industry News & Research, Uncategorized

This is a related article to: Hemochromatosis redefined Abstract Hemochromatosis (HC) is a genetically heterogeneous disorder in which uncontrolled intestinal iron absorption may…

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FDA approves once-weekly ALTUVIIIO™, a new class of factor VIII therapy for hemophilia A that offers significant bleed protection

Industry News & Research, Living with a Bleeding Disorder, Uncategorized

FDA approves once-weekly ALTUVIIIO™, a new class of factor VIII therapy for hemophilia A that offers significant bleed protection Paris and Stockholm – February 23, 2023 – The U.S. Food and Drug Administration (FDA) has…

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Introducing the WFH Gene Therapy Registry

Industry News & Research, Uncategorized

The new registry will enhance knowledge of gene therapy and help keep patients safe. The World Federation of Hemophilia (WFH) is a nonprofit organization…

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The Complexity of Unwinding Medicaid

Industry News & Research

The long-heralded Medicaid “unwinding” has begun. As previously reported, state Medicaid programs have, since the start of the COVID-19 pandemic, operated under a law that…

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BioMarin Update: FDA Extends PDUFA Target Action Date to June 30, 2023

Industry News & Research, Uncategorized

BioMarin Pharmaceutical Inc., a global biotechnology company dedicated to transforming lives through genetic discovery, announced that it received notice this afternoon from the…

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The Importance of Copay Assistance Protections: Awareness Grows

Industry News & Research, Living with a Bleeding Disorder

For over three decades, March has been designated “Bleeding Disorders Awareness Month.” HFA and member organizations across the country mark the occasion…

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FAQ: Proposed Changes to the FDA Blood Donation Policy

Industry News & Research, Uncategorized

Answering Your Questions on the recent FDA blood donation policy revisions. Answering Your Questions on the Proposed Change to the FDA’s Blood…

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Aminocaproic Acid Manufacturer Shuttered Though Not Expected to Trigger Shortage

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder, Uncategorized

Aminocaproic acid, which helps prevent the premature breakdown of blood clots, is often used to treat more minor bleeds in the nose…

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Summit Emphasizes Pharmacovigilance in the Inherited Bleeding Disorders Community

Industry News & Research, Uncategorized

The NHF/HFA Safety Summit yielded a series of recommendations related to product safety in the inherited bleeding disorders community. Biomedical and pharmaceutical…

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uniQure Announces Published Trial Results for Approved Gene Therapy

Industry News & Research, Uncategorized

These results were based on the multi-year HOPE-B Trial program. uniQure recently announced publication of the clinical trial results associated with approval…

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New Medscape Activity to Help Institutions Offer Gene Therapy

Industry News & Research, Uncategorized

NHF is pleased to announce that its collaboration with Medscape continues with a new accredited educational activity designed to help healthcare providers…

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BioMarin Announces FDA’s Extended Review of Investigational Hemophilia Gene Therapy

Industry News & Research, Uncategorized

ROCTAVIAN™ is currently in multiple ongoing clinical trials to observe its safety and efficacy in adult patients with severe hemophilia A. On…

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What You Need to Know About Hemochromatosis

Industry News & Research, Living with a Bleeding Disorder, Uncategorized

This blood disorder affects more than 1 million Americans and has no cure, but there are effective treatments. Hemochromatosis, also known as…

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