News

The Low Cost of Being Female with a Bleeding Disorder?
Health and Well Being, Industry News & Research, Living with a Bleeding Disorder
Female hemophilia A patients and carriers have more frequent bleeds than males, yet a smaller proportion receive factor to prevent or stop them, a U.S….

Now Enrolling: Own Your Path
Industry News & Research
Are you a male, 18-29 years old, and on a prophy regimen for hemophilia treatment? You may qualify for a new program!…

Four New Documents from MASAC
Industry News & Research
The new guidelines cover recommendations for physical therapy, gene therapy readiness, vaccine guidance, and treatment. Download here. Source: National Hemophilia Foundation

New in Research: Updates on the “My Life Our Future” Project
Industry News & Research
Learn how this project from NHF, the American Thrombosis and Hemostasis Network, Bloodworks Northwest, and Bioverativ/Sanofi helped inform people with hemophilia on…

Inhibitor Risk Paper Informed by Genotyping Project
Industry News & Research
Between 2013-2017, the “My Life Our Future” (MLOF) project offered eligible individuals with hemophilia free genotyping, which is historically hard to access,…

Important: Action Needed Regarding Medicaid and Badgercare Eligibility
Advocacy & Legislation, Industry News & Research
As you may have heard, the Medicaid and CHIP (called Badgercare in Wisconsin) programs are re-starting eligibility reviews. Community members may receive…

FDA Requests Additional Information on Concizumab from Novo Nordisk
Industry News & Research
The company received a Complete Response Letter from the FDA seeking more information relevant to their BLA for concizumab. Novo Nordisk has…

Updates on Generic Desmopressin Product
Industry News & Research, Uncategorized
Desmopressin has the capacity to boost both factor VIII and von Willebrand factor levels. In July 2020 Ferring Pharmaceuticals suspended manufacturing of…

New Survey Spotlights Ongoing Concerns for People Living with Hemophilia B
Health and Well Being, Industry News & Research, Living with a Bleeding Disorder
Carefully controlled schedules. Undercurrents of uncertainty. Persistent pain. People who are living with hemophilia B, and those who love them, face a…

HTCs Participate in New CDC Community Counts Data Collection for COVID-19
COVID-19 / Coronavirus, Industry News & Research
Patients with bleeding orders may be asked some new questions during their next comprehensive clinic visit. COVID-19 information will now be collected…

Sanofi Announces Publication of Two Phase 3 Fitusiran Trials
Industry News & Research, Uncategorized
Fitusiran is being investigated for the prophylactic treatment of adults and adolescents with hemophilia A or B. Sanofi recently announced that results…

Hemochromatosis Classification: Update and Recommendations by the BIOIRON Society
Industry News & Research, Uncategorized
This is a related article to: Hemochromatosis redefined Abstract Hemochromatosis (HC) is a genetically heterogeneous disorder in which uncontrolled intestinal iron absorption may…

FDA approves once-weekly ALTUVIIIO™, a new class of factor VIII therapy for hemophilia A that offers significant bleed protection
Industry News & Research, Living with a Bleeding Disorder, Uncategorized
FDA approves once-weekly ALTUVIIIO™, a new class of factor VIII therapy for hemophilia A that offers significant bleed protection Paris and Stockholm – February 23, 2023 – The U.S. Food and Drug Administration (FDA) has…

Introducing the WFH Gene Therapy Registry
Industry News & Research, Uncategorized
The new registry will enhance knowledge of gene therapy and help keep patients safe. The World Federation of Hemophilia (WFH) is a nonprofit organization…

The Complexity of Unwinding Medicaid
Industry News & Research
The long-heralded Medicaid “unwinding” has begun. As previously reported, state Medicaid programs have, since the start of the COVID-19 pandemic, operated under a law that…

BioMarin Update: FDA Extends PDUFA Target Action Date to June 30, 2023
Industry News & Research, Uncategorized
BioMarin Pharmaceutical Inc., a global biotechnology company dedicated to transforming lives through genetic discovery, announced that it received notice this afternoon from the…

The Importance of Copay Assistance Protections: Awareness Grows
Industry News & Research, Living with a Bleeding Disorder
For over three decades, March has been designated “Bleeding Disorders Awareness Month.” HFA and member organizations across the country mark the occasion…

FAQ: Proposed Changes to the FDA Blood Donation Policy
Industry News & Research, Uncategorized
Answering Your Questions on the recent FDA blood donation policy revisions. Answering Your Questions on the Proposed Change to the FDA’s Blood…

Aminocaproic Acid Manufacturer Shuttered Though Not Expected to Trigger Shortage
Health and Well Being, Industry News & Research, Living with a Bleeding Disorder, Uncategorized
Aminocaproic acid, which helps prevent the premature breakdown of blood clots, is often used to treat more minor bleeds in the nose…

Summit Emphasizes Pharmacovigilance in the Inherited Bleeding Disorders Community
Industry News & Research, Uncategorized
The NHF/HFA Safety Summit yielded a series of recommendations related to product safety in the inherited bleeding disorders community. Biomedical and pharmaceutical…

uniQure Announces Published Trial Results for Approved Gene Therapy
Industry News & Research, Uncategorized
These results were based on the multi-year HOPE-B Trial program. uniQure recently announced publication of the clinical trial results associated with approval…

New Medscape Activity to Help Institutions Offer Gene Therapy
Industry News & Research, Uncategorized
NHF is pleased to announce that its collaboration with Medscape continues with a new accredited educational activity designed to help healthcare providers…

BioMarin Announces FDA’s Extended Review of Investigational Hemophilia Gene Therapy
Industry News & Research, Uncategorized
ROCTAVIAN™ is currently in multiple ongoing clinical trials to observe its safety and efficacy in adult patients with severe hemophilia A. On…

What You Need to Know About Hemochromatosis
Industry News & Research, Living with a Bleeding Disorder, Uncategorized
This blood disorder affects more than 1 million Americans and has no cure, but there are effective treatments. Hemochromatosis, also known as…