News

Late last year the FDA put a clinical hold on the program in response to a single trial participant who was diagnosed…

Biochemist Gordon Vehar, PhD, vice president of external innovation at BioMarin Pharmaceutical Inc., has been at the forefront of a scientific revolution….

You have been reaching out to us with your questions and concerns about the COVID-19 vaccines and we are grateful that you…

The Platelet Disorder Support Association recently recorded a patient education webinar on the new COVID-19 vaccines and immune thrombocytopenic purpura (ITP) As…

The focus of the HOPE-B trial is etranacogene dezaparvovec, uniQure’s investigational gene therapy candidate for individuals with severe and moderately severe hemophilia…

In the age of high deductibles and patient out-of-pocket expenditures, more and more people depend on copay assistance to afford their life-saving…

Spark Therapeutics announced preliminary data from part one of their ongoing phase 1/2 open-label, non-randomized, dose-finding study of SPK-8016, the company’s investigational…

Source: Joint statement from the European Hemophilia Consortium, the World Federation of Hemophilia, and the National Hemophilia Foundation Fitusiran update following EAHAD…

In this video, Kollet Koulianos from NHF’s Payer Relations team explains the significance of copay Accumulator Adjustment programs. Watch now. Source: National…

The guidelines were developed by panels of 32 individuals, including hematologists, people living with VWD, and scientists with expertise in guideline development…

The phase 3 trial currently includes 134 participants with hemophilia A, all of whom have received a single dose of the gene…

The Consolidated Omnibus Appropriations Bill, 2021, signed into law by President Trump on December 27, 2020 included a number of provisions important…

The National Hemophilia Foundation (NHF) will be hosting a series of weekly webinars every Wednesday at 1 p.m. CST (2 p.m. ET) beginning…

Learn about the potential benefits and risks, along with what to look out for when evaluating products. Read more hemaware.org

Milwaukee County Updates to the COVID-19 Dashboard Since the pandemic began in March, the Milwaukee County COVID-19 dashboard has provided residents with…

President Trump has issued a number of executive orders on drug pricing. We show which ones could affect people with bleeding disorders….

The CDC is recommending that healthcare workers and residents of nursing homes be the first to receive the new coronavirus vaccines. The…

The makers of two coronavirus vaccines, Pfizer and its German partner BioNTech, and Massachusetts-based Moderna, have applied to the FDA for emergency…

Leaders of Wisconsin’s Two Medical Schools Urge Everyone to Take Action During the COVID-19 Outbreak. Med School Leaders Urge Public to Stay…

Thirty three organizations, including NHF, urge elected officials to ensure all people living in the US have access to adequate and affordable health…

A joint statement of the World Federation of Hemophilia (WFH), European Haemophilia Consortium (EHC) and National Hemophilia Foundation (NHF). The WFH, EHC…

Twenty patient groups representing millions of Americans with pre-existing conditions are urging the U.S. Supreme Court to prioritize patient protections, including those…

Note: The My Life, Our Future Research Repository includes the largest bank of genomic and phenotypic data about people with hemophilia. While…

Note: This webinar explores the diagnosis and clinical management of patients with rare inherited bleeding and platelet disorders. The National Hemophilia Foundation…