News

Michigan Study Explores Gene Therapy Understanding in Hemophilia Community

Gene Therapy, Industry News & Research, Living with a Bleeding Disorder

Participate in Groundbreaking Michigan Study on Gene Therapy Awareness in the Hemophilia Community The National Bleeding Disorders Foundation is supporting an important…

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NBDF’s Patient Assistance Programs (PAPs) Listing Updated!

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

The National Bleeding Disorders Foundation’s (NBDF) HANDI program has updated the online Patient Assistance Programs (PAPs) listing. The PAPs resource page encompasses programs designed to…

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FDA Approves Subcutaneous Therapy for Hemophilia Patients with Inhibitors

Industry News & Research

The U.S. Food and Drug Administration (FDA) has approved Alhemo (concizumab-mtci) for routine prophylaxis to prevent or reduce the frequency of bleeding…

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Global Experts Create Blueprint for Future VWD Research

Industry News & Research

In a significant advancement for von Willebrand Disease (VWD) research and treatment, an international team of experts, including patients, clinicians, and researchers,…

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Investigational Sub-Q von Willebrand Disease Therapy Put on Fast Track

Industry News & Research

The U.S. Food and Drug Administration (FDA) has granted Fast Track designation to the investigational von Willebrand disease (VWD) therapy VGA039. The…

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Clinical Practice and Hemophilia Gene Therapy the Focus of New Accredited Activity

Gene Therapy, Industry News & Research

The National Bleeding Disorders Foundation (NBDF) is excited to announce a new online, enduring, and accredited educational activity available to healthcare providers….

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Washington Days 2025, NBDF’s Annual Advocacy Event, is March 5-7

Advocacy & Legislation, Industry News & Research

Are you ready to advocate for the bleeding disorders community? Join us at Washington Days 2025 for a powerful and impactful experience. Learn…

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Learn About the T.H.R.I.V.E. Campaign

Health and Well Being, Industry News & Research

The T.H.R.I.V.E. campaign is an initiative to educate individuals with bleeding disorders and their support networks about six key steps for leading…

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How to Protect Yourself from Fractures

Health and Well Being, Industry News & Research

Bone health isn’t necessarily top of mind — especially at younger ages — but it should be. One study revealed that people with…

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Beyond Medication: The Benefits of Physical Therapy for Chronic Pain

Industry News & Research, Pain Management

Chronic pain affects up to 58% of people with hemophilia, impacting mobility, mental health and daily activities. Recognizing this widespread issue, the…

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New Recommendations Issued on Bleeding Disorders Treatment, Bone Health and Mental Health

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

The National Bleeding Disorders Foundation (NBDF) has announced that three new documents have been issued by the Medical and Scientific Advisory Council…

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B Informed!

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

For thirty years, the Coalition for Hemophilia B has improved the quality of life for people with hemophilia B and their families…

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New Study Looks at GI Bleeding in von Willebrand Disease

Industry News & Research

A new study sheds light on the challenges of diagnosing and managing gastrointestinal (GI) bleeding in individuals with severe von Willebrand disease…

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Durability of FactorVIII Focus of New Hemophilia A Gene Therapy Study

Industry News & Research

CHOP Researchers Investigate Durability of Hemophilia A Gene Therapy Findings of a new preclinical study published online in Nature Communications may help address lingering…

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FDA Approves Pfizer’s HYMPAVZI for Hemophilia A and B Treatment

Industry News & Research

On October 11, 2024, Pfizer announced that the U.S. FDA approved HYMPAVZI™ (marstacimab-hncq) for routine prophylaxis to prevent or reduce the frequency…

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New Study Uncovers Breakthrough for Long-Term Hemophilia A Gene Therapy

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

 new preclinical study led by CHOP researchers, published in Nature Communications, offers promising insights into the long-term effectiveness of hemophilia A gene therapy….

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2025 World Hemophilia Day Theme Revealed

Health and Well Being, Industry News & Research, Living with a Bleeding Disorder

The World Federation of Hemophilia (WFH) announced the 2025 World Hemophilia Day theme: Access for All: Women and Girls Bleed Too. Learn…

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FDA Approves Pfizer’s HYMPAVZI for Hemophilia A and B Treatment without Inhibitors

Industry News & Research

Phil Gattone said, “We greatly appreciate Pfizer’s innovative efforts in developing this novel treatment option that addresses some of the ongoing challenges…

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Critical Policy Updates: Medicaid Changes, ACA Credits, and More

Advocacy & Legislation, Health and Well Being, Industry News & Research

Dive into NBDF’s August 2024 Government Relations Update for essential information on Medicaid unwinding, ACA premium tax credits, NIH reform, and state-level…

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Product Update from NovoNordisk

Industry News & Research

A manufacturing deviation at NovoNordisk’s Danish facility has led to potential underfilling of vials for NovoSeven©, NovoEight©, and Esperoct© – crucial treatments…

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VWD: A Glimpse into Tomorrow’s Treatments

Industry News & Research, Living with a Bleeding Disorder

A session on von Willebrand Disease (VWD) at the National Bleeding Disorders Foundation Conference this past summer, highlighted patient-driven treatment advancements and…

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Learn More About Gene Therapy

Gene Therapy, Health and Well Being, Industry News & Research

A comprehensive document identifies 50 various publications about gene therapy, much of it accessible for parents and patients. The list includes: FAQs,…

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Gene Therapy’s Slow Start

Gene Therapy, Health and Well Being, Industry News & Research

Multimillion-dollar gene therapies were long awaited and desired, but patients were unsure whether insurance would cover the costs. So far, very few patients are…

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Attention Clinicians! New Bleeding Disorders Education Available from IHS

Industry News & Research

These new medical-based webinars will speak to key topics relevant to the care of patients with inherited bleeding disorders. NBDF is excited…

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