Countries Across the Globe Join the Gene Therapy Race
Canada Considers Funding Patient Gene Therapy; India Conducts First Human Clinical Trials for Hemophilia A
An excellent article explains how Canada’s government is considering paying $3-4 million per person for gene therapy, and why living successfully with hemophilia depends on where one is born. Read here.
Scientists at the Christian Medical College (CMC) Vellore (in south India) have successfully conducted the country’s first human clinical trial of gene therapy for hemophilia A. The clinical trials involved deploying a novel technology of using a lentiviral vector to express a FVIII transgene in the patient’s own hematopoietic stem cell, which will then express FVIII from specific differentiated blood cells. India is home to the second-largest population of patients with hemophilia, an estimated 136,000.
Source: Communiqué, LA Kelley Communications, Inc., April 2024